Dear CTNNB1 community,
We took a short break at the beginning of the year due to an exceptionally busy period, but we’re excited to be back with a new edition of our monthly
newsletter. 🗞️
This issue brings both hope and honesty. 💙
We’re pleased to share key advancements in our gene therapy program, including early post-treatment observations from the first patient and the initiation of screening for the next one. This issue also covers progress in our Natural History Study, upcoming conference developments, newly awarded grants, and continued efforts to expand research. At the same time, we highlight the critical importance of sustained funding to ensure successful clinical translation. 🚀
The CTNNB1 Team
👉 Download the March 2026 Newsletter (PDF)
Best,
The CTNNB1 Team