Author name: Bruno Ramalho

Dear CTNNB1 community, As we prepare to gather once again for our annual conference, this month’s newsletter is filled with exciting updates from across our global community. From major research milestones and clinical trial progress to preparations for the upcoming conference in Barcelona, there is much to celebrate and look forward to. Inside, you’ll find highlights from recent […]

Dear CTNNB1 community, This month’s newsletter brings several important milestones and updates from across the CTNNB1 community. We share exciting progress from the GAIN clinical trial, including the successful treatment of the second patient in the world with our investigational gene therapy URBAGEN intended to treat CTNNB1 syndrome.  We also reflect on recent community activities, from the ESGCT Summer School in Coimbra